Statistical Topics in Gene Therapy

What if we could target genetic diseases at their root, offering lifelong cures instead of temporary solutions? And what role do statisticians play in making this breakthrough possible? In this episode of The Effective Statistician, I dive into the fascinating world of gene therapy—an area packed with both promise and complexity. I'm thrilled to finally cover this revolutionary field with two expert guests, Avery McIntosh from Pfizer and Alex Sverdlov from Novartis. Together, we break down the science behind gene therapies, explore the ethical and logistical challenges, and reveal how statisticians drive these life-changing treatments forward. So, how close are we to curing diseases through gene therapy? Let’s jump in and find out.